FDA priority review of pz-cel Biologics License Application (BLA) progressing with Prescription Drug User Fee Act (PDUFA) target action date of ...

Arapahoe County shared photos of the squirrel Wednesday and said its Open Spaces Department believes the squirrel is ...

Galzin (zinc acetate capsules) is now available for maintenance treatment of patients with Wilson disease who have been initially treated with a chelating agent.

On March 18, Daddario shared an adorable, unfiltered photo of her and her son with two birthday cakes. She shared the ...

Nephronophthisis (NPH) is a recessive cystic kidney disease responsible for 10% to 20% of pediatric end-stage renal disease cases. NPHP1 (nephrocystin 1) is the most frequently implicated among over ...

INmune Bio's high-upside potential with CORDStrom for RDEB and XPro for Alzheimer's, offering up to 144.8x returns. Click ...

Lamellar ichthyosisis one of several types of skin disorders (skin disorder) which is calledichthyosis. Ichthyosisis a term for a severe and persistent dry skin condition that almost always begins in ...

Adeno-associated virus (AAV)–mediated gene therapy was one of the focal points of this year's Muscular Dystrophy Association conference. Here, Barry Byrne, MD, PhD, University of Florida, speaks to ...

With decades of experience in pharmaceutical development and extensive genetic medicine expertise, Doug E. Williams, Ph.D., and Murray Stewart, ...

The day honoring the patron saint of Ireland is a global celebration of Irish heritage. And nowhere is that more so than in the United States, where parades take place in cities around the country and ...

Every dog deserves a loving forever home. No matter where the dog came from. If you are adopting a dog from a shelter, ...