SynaptixBio announces milestone with selection of candidate drug to treat rare disease H-ABC: Our Bureau, Bengaluru Friday, June 20, 2025, 12:30 Hrs [IST] Oxford-based SynaptixBio ...

SynaptixBio announces a major milestone with SB H-19642 in the upcoming clinical trial for treating H-ABC disease.

Leukodystrophy isn’t just one disease; it’s actually a group of diseases that affect the central nervous system. Doctors are discovering new forms of leukodystrophy all the time, but experts ...

Metachromatic leukodystrophy, MLD for short, is a rare but highly debilitating neurodegenerative disease. It is noteworthy for its difficulties and the potential promise the latest research offers ...

Metachromatic leukodystrophy is a rare genetic disorder that affects between 1 and 9 people out of 100,000 and manifests itself mainly in childhood and adolescence—with 10 to 20% of cases ...

Please provide your email address to receive an email when new articles are posted on . Biotech firm SynaptixBio has entered into a licensing agreement with the Children’s Hospital of ...

Claire Edwards has AARS2 leukodystrophy which affects the brain and nervous system A man is desperately trying to raise awareness of a rare genetic disorder affecting his wife. Paul Edwards said ...

Leukodystrophy is a group of rare genetic neurological diseases that cause the sufferer to revert to a child-like state. In a Channel 4 documentary, The Curious Case of the Clark Brothers, living ...