Panelists discuss how recent advancements in muscular dystrophy treatment have evolved toward truly disease-modifying ...

Medcare’s approach goes beyond clinical excellence. Patients benefit from a multidisciplinary team that includes experts in ...

Liver damage is a well-recognised complication of gene therapies based on adeno-associated virus (AAV) vectors, and other ...

June 17th 2019EP. 8: Patient Perspective and Payer Perspective of SMA June 17th 2019EP. 9: Payer Diagnostic Criteria and Prior Authorization of SMA June 17th 2019EP. 10: Prior Authorization and ...

Influencers are everywhere — but few can be more influential than those who educate and entertain millions of people by ...

Shad’s R&R Canadian aftermarket fundraiser exceeded its stretch goal of $6 million dollars in cumulative funds raised, a ...

Taevion Norris’ graduation took place in Lurie Children’s Hospital because he was too sick to attend the ceremony. The hospital and staff went the whole nine yards. As “Pomp and Circumstance” played, ...

编者按：随着神经系统疾病在全球范围内负担的持续加重，人们对有效治疗复杂中枢神经系统（CNS）疾病的疗法需求日益迫切。作为世界领先的神经科学转化研究创新企业之一，罗氏（Roche）站在应对这一挑战的第一线——过去十年间，罗氏在为患者带来创新疗法方面取得了重大进展，其针对多发性硬化、脊髓性肌萎缩、视神经脊髓炎和 ...

He faced a future of never being able to walk again and having to breathe with a ventilator. But things changed temporarily for then 25-year-old Nagel when he became the first person to have a device ...

Eric Dane, the Hollywood actor, has been diagnosed with Amyotrophic Lateral Sclerosis (ALS). He opened up about the impact ...

The future of many hospice facilities and care homes is under threat from a “tragedy” can only be avoided by the defeat of the assisted dying legislation ...

I am upgrading Dyne Therapeutics stock to a 'Buy' rating due to promising late-stage DM1 and DMD drug candidates and ...