Panelists discuss how spinal muscular atrophy is an autosomal recessive genetic disease affecting motor neurons with 3 ...

A girl was diagnosed with a rare muscle -wasting condition after she stopped crawling as a baby. Ellie Soares, 11, seemed ...

DataM Intelligence | competitive Intelligence Spinal Muscular Atrophy treatment is evolving fast, with gene therapy, oral drugs, and next-g ...

Scholar Rock’s investigational spinal muscular atrophy drug helped patients taking Eli Lilly’s obesity blockbuster Zepbound ...

Many SMA patients continue to see gains in motor function with long-term Spinraza treatment, a real-world study from ...

Newborn with SMA gene mutation receives presymptomatic treatment at SAT Hospital, a rare step in managing rare diseases.

In combination with Eli Lilly’s tirzepatide, marketed as Zepbound for obesity, Scholar Rock’s monolonal antibody helped ...

"Everything we do is for the cause. It's a cause that's bigger than us. It's all for the kids. It's more than a football game ...

Shares of Scholar Rock (SRRK) soared 16% on Wednesday after the company announced that its investigational drug Apitegromab, ...

Thiruvananthapuram: For the first time in India, pre-symptomatic treatment to an infant, diagnosed with spinal muscular ...