Scholar Rock's Apitegromab excels in Phase 2 trials, aiding muscle preservation with Tirzepatide. Click here to read why I ...

Panelists discuss how spinal muscular atrophy is an autosomal recessive genetic disease affecting motor neurons with 3 ...

Scholar Rock (NASDAQ: SRRK), a late-stage biopharmaceutical company focused on developing and commercializing apitegromab for patients with spinal muscular atrophy (SMA) and other severe and ...

Jaipur: The life of 20-month-old Kartik hangs in balance. Diagnosed with spinal muscular atrophy (SMA), a rare and life-threatening neuromuscular dise.

"Everything we do is for the cause. It's a cause that's bigger than us. It's all for the kids. It's more than a football game ...

The use of salbutamol may improve upper limb strength and aid breathing in young children with spinal muscular atrophy, an ...

As Dr. Geary transitions out of his role, he will continue as a strategic consultant through 2026 to ensure continuity. Ionis ...

A 'fragile' girl's life has been transformed thanks to "caring and loving" staff at a hospice. Ellie, 12, from Salisbury, Wiltshire, has a rare life-limiting muscle wasting condition called Spinal ...

When young Lilah Lamont goes to school her nurse accompanies. The nurse helps her get into and out of her wheelchair, and ...

A girl was diagnosed with a rare muscle -wasting condition after she stopped crawling as a baby. Ellie Soares, 11, seemed ...

For 4-year-old Stella Duran, playing outside with her older sister, family and friends is one of life’s greatest joys. Now, ...