The reported dismissal of high-ranking CBER officials Nicole Verdun and Rachael Anatol resurfaced lingering concerns about how gene therapies will be regulated under new FDA leadership.

Researchers have found a promising new method for gene therapy. They successfully restarted inactive genes by bringing them ...

Beam Therapeutics shows promising BEACON trial results in SCD, backed by strong cash reserves and pipeline momentum. See why ...

Eli Lilly will buy Boston-based Verve Therapeutics, Inc. in a billion dollar deal with plans to advance Verve's new line of ...

By Christy Santhosh and Bhanvi Satija (Reuters) -Shares of Sarepta Therapeutics slumped 42% on Monday after a second patient who had received its gene therapy, Elevidys, died in a span of three months ...

A second patient with Duchenne muscular dystrophy has died from acute liver failure after receiving the gene therapy Elevidys ...

BIRAC and Miltenyi Biotec India have joined forces to elevate India's standing in cell and gene therapy (CGT). The ...

You can reach Jason on Signal at JasonMast.05. What will the Trump administration mean for gene therapy? Researchers, advocates, and executives got a glimpse of the answer Thursday, as the Food ...

A research team at the University of Osaka has unveiled the molecular mechanism behind genome ejection from adeno-associated ...

Our Bureau, Bengaluru Thursday, June 19, 2025, 15:35 Hrs [IST] ...

Oregon Health Plan (OHP) members will see increased access to lower-cost, lifesaving cell and gene therapies. The state is ...