From today, the updated indication for TRIKAFTA is as follows: TRIKAFTA is indicated for the treatment of cystic fibrosis in patients aged 2 years and older who have at least one F508del mutation in ...

In March 2025, Vertex Pharmaceuticals Incorporated announced a study is to evaluate the safety, and tolerability and efficacy ...

Vertex Pharmaceuticals Incorporated VRTX stock has plunged 25.3% this year so far against the industry’s 5.4% increase. VRTX ...

Cystic fibrosis (CF) patients could be given access to a new drug on the NHS by the end of the year if it is given the green ...

A MIRACLE pill that’s been shown to help with many of the symptoms of cystic fibrosis (CF) has been approved for thousands of ...

The Hospital for Sick Children. "Newly uncovered mechanism could drive next-gen cystic fibrosis treatments." ScienceDaily. ScienceDaily, 13 March 2025. <www.sciencedaily.com / releases / 2025 / 03 / ...

A new research project focusing on rare genetic mutations that are linked to cystic fibrosis just received $600,000 in ...

Studying how proteins cluster and organize themselves at the cell membrane could pave the way for innovative cystic fibrosis ...

A new study from The Hospital for Sick Children (SickKids) reveals the process underlying protein organization on cell ...

A new study from The Hospital for Sick Children (SickKids) reveals the process underlying protein organization on cell membranes, a finding which ...

A recent review published in the journal Engineering delves into the significant advancements and potential of CRISPR ...

Cystic fibrosis (CF) is a life-threatening autosomal recessive disease affecting over 160,000 people worldwide. CF is caused by loss-of-function mutations in the CF transmembrane conductance regulator ...