The mother of a terminally ill 11-year-old has spoken of her heartbreak at knowing her daughter may not live past her teens.

The community has rallied around the family of a young girl diagnosed with an extremely rare degenerative condition.

Anna Lowri Roberts is one of 39 people in the UK with CLN3 Batten Disease The mother of a terminally ill 11-year-old has spoken of her heartbreak at knowing her daughter may not live past her teens.

James Murray is running the Inverness Half Marathon next month to support Sophie’s Story, set up for little Sophie Mason who ...

James Murray is running the Inverness Half Marathon next month to support Sophie’s Story, set up for little Sophie Mason who ...

Communiqué de la société THERANEXUS du 23/01/2025 - THERANEXUS ANNOUNCES ITS FINANCIAL CALENDAR FOR 2025 ...

Theranexus SA ( ($FR:ALTHX) ) has issued an update. Theranexus has announced its financial communication agenda for 2025, detailing key dates for ...

June 10, 2024 — Scientists have grown 'mini-guts' in the lab to help understand Crohn's disease, showing that 'switches' that modify DNA in gut cells play an ... Major Cause of Inflammatory ...

Which Market Leaders Have Staked a Claim in the Brineura Market? The brineura market is served by several key industry players, with major companies including BioMarin Pharmaceutical Inc. leading the ...

Also known as Batten disease, CLN2 is a progressive condition caused by the deficiency of the enzyme tripeptidyl peptidase 1. This results in the abnormal storage of proteins and lipids in neurons ...

In a report released today, Luca Issi from RBC Capital maintained a Buy rating on Lexeo Therapeutics, Inc. (LXEO – Research Report), with a ...