Elevidys has been given full approval to treat ambulatory patients with DMD, with an accelerated approval in non-ambulatory ...

Sarepta reported a second death in a patient who had received its gene therapy, which raised concerns about the safety and ...

Duchenne muscular dystrophy is characterized by a mutation in the DMD gene that leads to a lack of dystrophin and muscle loss ...

Sarepta has issued a safety update regarding Elevidys (delandistrogene moxeparvovec-rokl) following a second reported case of acute liver failure resulting in death.

The first procedure in the world designed to treat a patient using a bioengineered external liver was recently performed by a team at Intermountain Medical Center.

The only option left for the doctors was liver transplantation and Anakendu's mother came to her rescue by volunteering to ...

A second patient with Duchenne muscular dystrophy has died from acute liver failure after receiving the gene therapy Elevidys ...

The FDA is investigating two deaths in non-ambulatory Duchenne muscular dystrophy patients who received a Sarepta gene ...

Introduction. Acute liver failure (ALF) is not a diagnosis but a clinical syndrome. ALF was initially characterized in adults with biochemical evidence of severe hepatic dysfunction (e.g ...

Acute-on-chronic liver failure (ACLF) is a syndrome characterised by acute decompensation of chronic liver disease associated with organ failures and high short-term mortality. Alcohol and chronic ...

Your liver grows as you age, though certain health conditions, including acute hepatitis and fatty liver disease, can cause an enlarged liver. A large liver doesn’t always cause symptoms. The ...

The commercial and clinical use of Elevidys was discontinued after two fatal cases of acute liver failure.