Elevidys has been given full approval to treat ambulatory patients with DMD, with an accelerated approval in non-ambulatory ...

Sarepta reported a second death in a patient who had received its gene therapy, which raised concerns about the safety and ...

Duchenne muscular dystrophy is characterized by a mutation in the DMD gene that leads to a lack of dystrophin and muscle loss ...

The first procedure in the world designed to treat a patient using a bioengineered external liver was recently performed by a team at Intermountain Medical Center.

The FDA is investigating two deaths in non-ambulatory Duchenne muscular dystrophy patients who received a Sarepta gene ...

Use precise geolocation data and actively scan device characteristics for identification. This is done to store and access ...

Hepatitis A outbreak in popular European destinations has sickened thousands, primarily affecting unvaccinated individuals ...