A new study by Mayo Clinic Comprehensive Cancer Center researchers found that the presence of a specific genetic ...

Beam Therapeutics reported promising Phase 1/2 data for BEAM-302, demonstrating durable gene correction for AATD. See why I ...

Adverse genetic mutations can cause harm and are due to various circumstances. 'Jumping genes' are one cause of mutations, but cells try and combat them with a specialized RNA called piRNA.

Early research shows a one-time gene therapy has potential for addressing both the liver and lung disease that patients with ...

The small study in patients with a rare disorder that causes liver and lung damage showed the potential for precisely ...

Parkinson’s disease (PD) affects nearly 2% of adults over 65, making it the second most common neurodegenerative disorder. It ...

Although cystic fibrosis is a single gene mutation, there are more than 1,000 different ways the CFTR gene can mutate in ...

Scientists say a concerning genetic mutation has appeared in H5N1 bird flu infected cats living in a New Jersey suburb of New ...

Genetic and genomic testing guide breast cancer risk assessment and treatment, as discussed by Dr. Mark Robson at the Miami ...

Preclinical data with the investigational gene therapy INS1202 show improvements in survival and motor performance in ALS.

Having two copies of the MTHFR gene mutation may raise your risk for certain health conditions, though more research is needed. You may have the mutation and not find out unless you undergo ...

But in about 5% to 10% of cases, the cause is hereditary. This means that the cancer is due to a gene change, called a “mutation,” that’s passed down from a parent. Researchers have ...