As Rare Disease Day is commemorated on 28 February, experts discuss the barriers to gene therapy access for some rare ...

However, research for some rare conditions, such as those due to inborn errors of metabolism, is stagnating due to logistical issues. The inborn errors of metabolism is a group of rare genetic ...

Inborn Errors of Metabolism Drug Development 2020 is dedicated to addressing these challenges to ensure that drug developers can achieve their full commercial potential. Access the full event ...

My consciousness freshly raised and my mind spongier than ever, I spent my evenings imbibing the no-nonsense feminism of ...

Directed by Sukumar, Pushpa 2: The Rule hit theaters on December 5, 2024 and quickly became one of the highest-grossing Indian films. The film, starring Allu Arjun alongside Rashmika Mandanna has ...

You will be able to get a quick price and instant permission to reuse the content in many different ways. Inborn errors of metabolism are a heterogeneous group of conditions which frequently cause ...

Primary immunodeficiencies are not as rare as they used to be, James Fernandez, MD, PhD, told Healio, and practicing ...