SpliceBio, a clinical-stage genetic medicines company, announced that it has dosed the first patient in the phase ½ Astra study of SB-007, a dual adeno-associated viral vector, for the treatment of ...

MILAN, March 31, 2025 — AAVantgarde Bio (AAVantgarde), a clinical-stage biotechnology company, in collaboration with the Telethon Institute of Genetics and Medicine (TIGEM), announces the publication ...

This CT softball pitcher, who is visually impaired, helped her team to the state championship game last season and her team ...

MILAN, March 31, 2025 (GLOBE NEWSWIRE) -- AAVantgarde Bio (AAVantgarde), a clinical-stage biotechnology company, in collaboration with the Telethon Institute of Genetics and Medicine (TIGEM), ...

Tilly Dowler, from Castle Donington, Derbyshire, was diagnosed with Stargardt disease, a rare genetic eye condition that causes loss of central vision when she was 15 years old. Symptoms usually ...

MILAN, March 31, 2025 (GLOBE NEWSWIRE) -- AAVantgarde Bio (AAVantgarde), a clinical-stage biotechnology company, in collaboration with the Telethon Institute of Genetics and Medicine (TIGEM), ...

so approval in Stargardt disease would prompt the pricing negotiation mechanism. Alnylam's earlier plan was to start trials of the drug before the end of this year in the genetic eye disease ...

in collaboration with the Telethon Institute of Genetics and Medicine (TIGEM), announces the publication of their preclinical research in Stargardt’s disease in Science Advances, a prestigious ...

At Prime Minister’s Questions, Sir Keir joked that the golden retriever did not look ‘particularly interested’ in what he had ...