Panelists discuss how recent advancements in muscular dystrophy treatment have evolved toward truly disease-modifying ...

Wasting of muscle tissue can also occur with malnutrition and various nerve or muscle-related health conditions such as ...

Medcare’s approach goes beyond clinical excellence. Patients benefit from a multidisciplinary team that includes experts in ...

Muscular dystrophy can appear in infancy up to middle age or later, and its form and severity are determined in part by the age at which it occurs. Some types of muscular dystrophy typically ...

The test stimulation of the spinal cord was successful in 24 patients; the other 12 patients did not receive implanted stimulators. In an intention-to-treat analysis, the group assigned to receive ...

These data demonstrate the breadth of Roche’s neuromuscular portfolio across spinal muscular atrophy (SMA) and Duchenne muscular dystrophy (DMD). “These longer-term results are encouraging for people ...

Although multiple sclerosis (MS) and muscular dystrophy (MD) are both debilitating ... that affects the central nervous system (CNS)—the brain, spinal cord, and optic nerves.

Cleveland Clinic: “Spinal Muscular Atrophy.” Muscular Dystrophy Association: “Spinal Muscular Atrophy: SMA.” Genetic and Rare Diseases Information Center: “Spinal muscular atrophy type 3.” ...

Newly approved SMA therapies show promise but face global accessibility challenges, widening healthcare disparities due to high costs and limited availability. Newborn screening for SMA is ...

Steiner added, “For patients with spinal muscular atrophy specifically ... study of patients with SMA or Duchenne and Becker muscular dystrophy. Another similar finding between the studies ...

“Muscular Dystrophy Association celebrates continued advancements in SMA treatment, ensuring patients have access to effective and convenient therapies,” said Sharon Hesterlee, PhD ...

Liver damage is a well-recognised complication of gene therapies based on adeno-associated virus (AAV) vectors, and other ...