An England-wide study of over 58 million people has identified eight rare diseases that carry significantly increased risks for COVID-19-related mortality in fully vaccinated individuals.
Inspired by the rare disease community’s passionate drive to advance policies that provide equitable access to care, UCB spearheaded Aspire4Rare: a global initiative supporting the development of ...
High-quality evidence for the treatment of very rare diseases: IQWiG is involved in the EU project RealiseD Developing clinical trials to provide good evidence for very rare diseases, so that ...