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Blue cone monochromacy is a rare X-linked retina disorder. It causes a complete or near-complete loss of function in the L- and M-cones responsible for color vision.
rod monochromacy, in which none of the three types of cones, L (long wavelength-sensitive)-, M (middle wavelength-sensitive)- or S (short wavelength-sensitive)-cones, are functional; (2 ...
ADVM-062, a novel gene therapy candidate, received orphan drug designation from the FDA for the treatment of blue cone monochromacy, according to a press release from Adverum Biotechnologies.
Adverum Biotechnologies Granted Orphan Drug Designation by FDA for Gene Therapy Candidate in Preclinical Development for the Treatment of Blue Cone Monochromacy Published Jan 4, 2022 8:00am EST ...
(HealthDay)—Imagine a world in black and white. That's the plight of people with an extremely rare condition called blue cone monochromacy, an inherited eye disease that renders people unable to ...
Blue Cone Monochromacy, a rare form of colorblindness, affects 1 in 100,000 individuals. It leads to poor or no color discrimination, which is why the photo above looks sort of like it’s been ...
7m8-L-opsin), a novel gene therapy product candidate being developed as a potential single intravitreal (IVT) administration for blue cone monochromacy ... Laurent Fischer, M.D., president ...
06, 2016 (GLOBE NEWSWIRE) -- Applied Genetic Technologies Corporation (Nasdaq:AGTC), a biotechnology company conducting human clinical trials of adeno-associated virus (AAV)-based gene therapies for ...