Genetic medicines could treat certain diseases, however, the current delivery systems available—viral vectors and lipid nanoparticles (LNPs)—pose unique challenges for gene therapy applications. For ...

Researchers are enhancing the best features of AAV capsids and overcoming their limitations to accelerate gene-based therapies.

The majority are in the very early preclinical stage of development, but applications for regulatory approval have been ...

The California Institute for Regenerative Medicine has awarded a $6 million grant to USC investigators pioneering a new first ...

NIS gene delivery into medullary and follicular ... which allows the clinician to pursue therapeutic strategies, including gene therapy, that might ablate normal as well as malignant thyroid ...

International collaborations, refined gene-editing protocols, and targeted immunologic maneuvers keep the cancer gene therapy ...

For the last 10 years, the only effective treatment for hypophosphatasia (HPP) has been an enzyme replacement therapy that ...

In two new papers, researchers from The Jackson Laboratory (JAX) report the successful use of two approaches -- gene therapy ...

Nandita Vijayasimha, Bengaluru Wednesday, January 29, 2025, 08:00 Hrs [IST] ...