MSC-based strategies should provide practical advantages ... their activities might be further enhanced via targeted gene therapy Delivery of MSCs might be achieved either by direct intra ...
Key Laboratory of Bio-chemistry Engineering - The State Ethnic Affairs Commission-Ministry of Education, Dalian Nationalities University, Dalian, China. State Key Laboratory of Fine Chemicals, Dalian ...
An in vivo base editing approach targeting the PRNP gene led to a 52% increase in the lifespan of mouse models inoculated with the most common sporadic and genetic types of human pathogenic prion ...
Advances in CRISPR technologies promise to accelerate the burgeoning pipeline of gene-editing therapies and broaden access to these disease-altering therapies.