Trump health officials signal eased FDA rules for rare disease gene therapy, but concerns linger over safety, oversight, and ...

Our Bureau, Bengaluru Thursday, June 19, 2025, 15:35 Hrs [IST] ...

By Bhanvi Satija and Christy Santhosh (Reuters) -Shares of Sarepta Therapeutics closed down as much as 42% to hit a nine-year low of $18.30 on Monday after a second death of a male teenage patient who ...

A second patient with Duchenne muscular dystrophy has died from acute liver failure after receiving the gene therapy Elevidys ...

Findings highlight the advantages of Adolore’s approach for the delivery of proprietary gene therapy directly to specialized ...

Gene therapy is a revolutionary field in modern medicine, offering transformative potential to treat and potentially cure a wide range of genetic and acquired diseases. By addressing the root ...

Supply chains for a new generation of therapies are complex, costly, and require meticulous management to ensure patient ...

BIRAC and Miltenyi Biotec India have joined forces to elevate India's standing in cell and gene therapy (CGT). The ...

In the first webinar, Understanding the Future of Cell and Gene Therapy, Rebecca Hulinsky, MS, CGC, director, health plan genomics strategy and solutions, Quest Diagnostics, explained genetic ...

A research team at The University of Osaka has unveiled the molecular mechanism behind genome ejection from adeno-associated virus (AAV) vectors, a ...

In comments posted in response to the Trump administration’s pharma tariff investigation, companies and industry groups offered solutions to ease the impacts if the plan must go ahead.

Regenxbio said Thursday that its experimental gene therapy for Duchenne muscular dystrophy was administered to two more boys and produced high levels of a miniaturized version of the protein ...