资讯

Galactosemia is a rare genetic condition that prevents babies from processing galactose, an important sugar in breast milk. Though the disease can cause many issues, it’s easily diagnosed and ...
Galactosemia is an inherited genetic disorder of metabolism where the body is unable to metabolize a sugar called galactose. Galactose forms half of the sugar lactose, which is found in milk. The ...
Galactosemia is a rare genetic disorder that causes an inability to digest galactose, which is a breakdown product of lactose. Lactose is one of the main carbohydrates in milk.
Nearly three months after an experimental treatment for classic galactosemia was rejected by the US Food and Drug ...
The NDA included data from the phase 1/2 ACTION-Galactosemia study (ClinicalTrial.gov Identifier: NCT04117711) and the phase 3 ACTION-Galactosemia Kids trial (ClinicalTrial.gov Identifier ...