The company has approved medicines that treat the underlying causes of multiple chronic, life-shortening genetic diseases cystic fibrosis, sickle cell disease and transfusion-dependent beta ...

Hydroxyurea remains effective long-term in reducing emergency department visits and hospital days for children living with sickle cell disease (SCD), according to new research published in Blood ...

While both sickle cell trait and sickle cell disease involve mutations in the haemoglobin gene, they are fundamentally different in terms of symptoms, severity, and impact on daily life.

People with sickle cell disease are immunocompromised, which means they have an increased risk of infection. For this reason, immunizations are an important part of complete sickle cell care. This ...

A new study shows that hydroxyurea, an oral drug, safely and effectively manages sickle cell disease in children. Kids who took the medication had fewer hospital visits and better health outcomes.

Two of the most commonly known symptoms of sickle cell disease are a vaso-occlusive crisis (perhaps the best-known symptom) and fatigue. But others aren’t so well-known; in fact, I’d say most people ...

Limited awareness about the need to know one’s sickle cell genotype is affecting mass screening for the disease. Sickle cell disease is a congenital blood disorder that presents with the production of ...

Following a breakthrough 'cure' for sickle cell disease being approved on the NHS, the Mirror sat down with four British ...

The NHS had also reached a deal in August 2024 to provide exa-cel for eligible patients with transfusion-dependent beta-thalassaemia. Sickle cell disease is caused by a gene mutation that results in ...

Sickle cell disease is a chronic, inherited blood disorder that affects millions of people worldwide. It is characterised by the production of abnormally shaped red blood cells, which can block ...