The company has approved medicines that treat the underlying causes of multiple chronic, life-shortening genetic diseases cystic fibrosis, sickle cell disease and transfusion-dependent beta ...

A new study shows that hydroxyurea, an oral drug, safely and effectively manages sickle cell disease in children. Kids who took the medication had fewer hospital visits and better health outcomes.

Sickle cell disease is a chronic, inherited blood disorder that affects millions of people worldwide. It is characterised by the production of abnormally shaped red blood cells, which can block ...

The report revealed the urgent need for improvements in ambulance services for people living with sickle cell disease in London (Kirsty O’Connor/PA) People with an inherited blood disorder have ...

Sickle cell disease is a group of inherited disorders that affect hemoglobin, which is the major protein that carries oxygen in red blood cells. Normally, red blood cells are disc-shaped and flexible ...

Kennedy Jr. announced a landmark initiative to expand access to cutting-edge treatments for sickle cell disease, a genetic blood disorder that disproportionately affects Black Americans ...

Nigerian families are said to be bearing secret burden of over N250bn per month on medical treatment of people living with sickle cell disease (PLWSCD). This is derived from a minimum of N25,000 ...

Kennedy Jr. said 35 states have agreed to participate in a federal pilot program aimed at helping Medicaid patients access costly gene therapies for sickle cell disease. The states represent about ...

Kennedy gave roughly five minutes of remarks to a packed ballroom in the Francis Marion Hotel, mainly focusing on progress in widening treatment access for sickle cell disease, a blood disorder ...