The interim data found one child in the Duchenne trial produced more than double the amount of the protein needed to maintain ...

This important study provides solid evidence that glucosylceramide synthase (GlcT), a rate-limiting enzyme for glycosphingolipid (GSL) production, plays a role in the differentiation of intestinal ...

Since Japan hosted the 2019 Rugby World Cup, the JRFU has launched the Japan Rugby 2050 initiative to raise the global appeal of Japanese rugby. One aspect of it is a robust, cloud-based approach to ...

By replacing the defective gene associated with Dravet syndrome in mice, scientists successfully alleviated symptoms without ...

Opus Genetics, Inc. (Nasdaq: IRD), a clinical-stage ophthalmic biopharmaceutical company developing important new therapies ...

Physicists in Germany have led experiments that show the inertia of electrons can form 'tornadoes' inside a quantum semimetal ...

When massive stars explode as supernovae, they can leave behind neutron stars. Other than black holes, these are the densest ...

Analysis - Chimpanzees are humans' closest living relatives, sharing over 98% of our DNA. They are endangered, with fewer ...

To break free from algorithmic loops, researchers and analysts must move toward living foresight models, approaches that ...

ROCKVILLE, MD, USA I March 19, 2025 I REGENXBIO Inc. (Nasdaq: RGNX) today reported new, positive interim data from two additional patients in the Phase ...

Opus Genetics, Inc. (Nasdaq: IRD), a clinical-stage ophthalmic biopharmaceutical company developing important new therapies for the treatment ...