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Biogen has bolstered its pipeline by licensing ex-US rights to a drug for Dravet syndrome – a rare form of epilepsy – from Stoke Therapeutics in a deal that included an upfront payment of $165 ...
After Sergio was diagnosed with Dravet Syndrome, Isla quickly became one of Spain’s main advocates for rare ... Since late 2023, Madrid’s public healthcare system has used an adapted version of the ...
The drug is specially formulated to relieve symptoms but does not produce ... There is a need for new treatments for LGS and Dravet syndrome: both are serious and often resistant to the drugs ...
For millions of people worldwide, this isn’t just hypothetical – it’s their daily reality of living with Irritable Bowel Syndrome (IBS ... is a combination of symptoms caused by multiple ...
Such as Lennox-Gastaut Syndrome (LGS). There are fewer than 500 patients with it. About 100 people have Dravet syndrome.
If you’re experiencing eye discomfort without discharge, you may be wondering whether you have allergies or dry eye syndrome. While these two conditions share some similarities in symptoms ...
Internal bleeding, or hemorrhage, is a serious medical emergency that can result from trauma, underlying medical conditions, or complications from surgery. Internal bleeding symptoms include severe ...
TK2d is divided into 3 types based on the age of symptom onset 1: infantile-onset TK2d, childhood-onset TK2d, and late-onset TK2d. Life expectancy is shortest in infantile-onset TK2d and most ...
Unlike Down’s Syndrome, which can be screened for during pregnancy, symptoms of Angelman don’t appear until the baby is at least six months old. The condition usually "occurs by chance" during ...
Using data from adolescents in the EMPOWER and ENABLE studies, researchers found lanadelumab to be effective and safe prophylaxis against HAE attacks.
Actor Colin Farrell has opened up about the difficult decision to move his son James, who has Angelman syndrome, into a long-term care facility. In an interview this week the actor, 48 ...