Kebilidi is the first gene therapy approved by the FDA for administration directly into the brain, given via a cannula during a surgical procedure, and replaces the human dopa decarboxylase (DDC ...

† Department of Chemistry, University of Warwick, Coventry CV4 7AL, U.K. ‡ Department of Biochemistry, University of Cambridge, Cambridge CB2 1GA, U.K. § School of Chemistry and Manchester Institute ...