Early research shows a one-time gene therapy has potential for addressing both the liver and lung disease that patients with ...

The small study in patients with a rare disorder that causes liver and lung damage showed the potential for precisely ...

A new H5N1 bird flu mutation has appeared in a cluster of infected dairy cows. It's a genetic change that scientists say ...

Parkinson’s disease (PD) affects nearly 2% of adults over 65, making it the second most common neurodegenerative disorder. It ...

People have two copies of most of their genes, one from each parent. Mutations can change or silence one or both copies. In the case of the Syngap1 gene, research has shown that two working copies are ...

But in about 5% to 10% of cases, the cause is hereditary. This means that the cancer is due to a gene change, called a “mutation,” that’s passed down from a parent. Researchers have ...

Now, scientists have revealed that a newly discovered 'fat gene' could be to blame. Experts from the University of Cambridge say that a mutation to a gene called DENND1B reduces the ability ...

BEAM-302 "has set the bar for efficacy in this space," William Blair analysts wrote in an investor note on Monday.