In the first part of this series, we explored how early genetic screening and gene therapy transform the lives of newborns ...

Machine learning models have seeped into the fabric of our lives, from curating playlists to explaining hard concepts in a ...

As newborn screening and rapid DNA sequencing become routine, we are poised to catch and treat inherited diseases at their ...

The death of a patient in a trial of an experimental gene therapy casts new shadows over a technology once seen as the future ...

In comments posted in response to the Trump administration’s pharma tariff investigation, companies and industry groups ...

This study reveals the potential of engineered phage-IL-12 therapy in melanoma, enhancing immune response and tumor ...

The FDA has slapped a clinical hold on Rocket Pharmaceuticals’ pivotal gene therapy trial in response to a death. Rocket, ...

A patient in a Rocket Pharmaceuticals gene therapy trial for a rare heart condition has died, the company said.

Advancements in gene therapy for Duchenne muscular dystrophy (DMD) have improved the outlook for some patients, but further ...

Rocket Pharmaceuticals Inc (NASDAQ:RCKT) on Tuesday announced an update related to RP-A501, its investigational gene therapy ...

The FDA has placed a clinical hold on the study while Rocket works with trial monitors and experts to investigate the cause ...