Base editing corrected a mutation that causes macular degeneration, highlighting the potential of gene therapy to treat ...

Dino Pecoraro decided to start boxing when he was 16 years old, just a few years after he had first noticed a change in his ...

The three main types of juvenile macular degeneration (JMD) include Stargardt disease, X-linked retinoschisis, and Best disease. These result from gene mutations. Early treatment may help preserve ...

Stargardt disease is an inherited retinal disorder caused by mutations in the ABCA4 gene. It is the most common form of juvenile macular degeneration, leading to progressive central vision loss and ...

SB-007 addresses the root cause of Stargardt disease with the potential to treat all patients across all ABCA4 mutations SB-007 is the first dual AAV gene therapy in clinical development for ...

Following a pre-specified interim analysis, the Data Safety Monitoring Board (DSMB) recommended the DRAGON trial, a pivotal Phase 3 trial in ...

Ocugen reported clinical trial progress and financial results, highlighting advancements in gene therapies for retinal diseases and recent FDA alignments. OCU410ST is a therapy for Stargardt ...