A 'fragile' girl's life has been transformed thanks to "caring and loving" staff at a hospice. Ellie, 12, from Salisbury, ...

A girl was diagnosed with a rare muscle -wasting condition after she stopped crawling as a baby. Ellie Soares, 11, seemed ...

Scholar Rock’s investigational spinal muscular atrophy drug helped patients taking Eli Lilly’s obesity blockbuster Zepbound ...

But now there is a ray of light. Lilah is scheduled for surgery on July 15 that will see a metal ring called a halo fastened ...

Shares of Scholar Rock (SRRK) soared 16% on Wednesday after the company announced that its investigational drug Apitegromab, ...

The baby from Ranaghat in Nadia is suffering from spinal muscular atrophy (SMA) Type I, a condition that causes progressive ...

In combination with Eli Lilly’s tirzepatide, marketed as Zepbound for obesity, Scholar Rock’s monolonal antibody helped ...

Newborn with SMA gene mutation receives presymptomatic treatment at SAT Hospital, a rare step in managing rare diseases.

DataM Intelligence | competitive Intelligence Spinal Muscular Atrophy treatment is evolving fast, with gene therapy, oral drugs, and next-g ...

Thiruvananthapuram: For the first time in India, pre-symptomatic treatment to an infant, diagnosed with spinal muscular ...

"Everything we do is for the cause. It's a cause that's bigger than us. It's all for the kids. It's more than a football game ...

Jaipur: The life of 20-month-old Kartik hangs in balance. Diagnosed with spinal muscular atrophy (SMA), a rare and life-threatening neuromuscular dise.