Ian MacPherson has had to overcome more challenges in his lifetime than any person should ever have to endure.

Compete for a Cause will host a 16-act talent competition at 6 p.m. on April 5 at Sheridan College for Pompe Disease patient ...

It is a detailed view of the brain like never seen before. In a significant technological leap, University of Florida ...

AI tool MetaVision3D creates detailed 3D maps of mouse brain metabolism, offering new insights into Alzheimer's and other ...

Aro Biotherapeutics has dosed the first patient in a Phase Ib trial of ABX1100, a novel treatment for late-onset Pompe disease (LOPD), a rare inherited disorder that causes progressive muscle ...

Sanofi's Genzyme rare diseases division already sells another enzyme replacement therapy for Pompe disease based on the recombinant enzyme alglucosidase alfa – sold as Myozyme in Europe and ...

Dr Anup Rawool, Consultant in Clinical and Cancer Genetics at Sahyadri Hospitals, Pune, discusses innovative therapies and ...

often fatal genetic disorder known as Pompe disease. Thanks to a lifesaving therapy pioneered by my own biotech start-up, Megan was by our side during that speech. She remains healthy and vibrant ...

Amicus Therapeutics benefits from strong revenue and limited competition. Learn why FOLD stock is a BUY, with a favorable ...