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rAAV2-ND1 基因疗法:为 Leber 遗传性视神经病变带来新希望
目前,LHON 的治疗手段极为有限,几乎可以说是束手无策。在众多研究中,多数聚焦于由最常见的 ND4 基因突变引起的 LHON,而对由较少见的 ND1 基因突变导致的 LHON 关注甚少。为了填补这一空白,湖北医药学院附属太和医院等机构的研究人员勇挑重担,开展了 ...
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