ARTHEx also has ATX-01 in preclinical testing for myotonic dystrophy type 2 (DM2). “Although DM2 is caused by a different mutation, it similarly results in the sequestration of MBNL proteins ...

1-2 Recent studies presented at the 2025 Muscular Dystrophy Association (MDA) Clinical & Scientific Conference shed light on these issues. Because myotonic dystrophy type 1 is a rare, progressive ...

Gottfried, who famously voiced Iago in Disney's 1992 classic Aladdin, had been dealing with recurrent ventricular tachycardia due to myotonic dystrophy type II, his longtime friend and publicist ...

More information: Preeti Kumari et al, Analysis of human urinary extracellular vesicles reveals disordered renal metabolism in myotonic dystrophy type 1, Nature Communications (2025). DOI: 10.1038 ...

The comic's widow, Dara Gottfried, says a portion of sales of 'Still Screaming' will benefit the Gilbert Gottfried Myotonic Dystrophy Type 2 Research Fund By Frank DiGiacomo Editor Gilbert ...

DYNE-101 Program Targeting Patients With Myotonic Dystrophy Type 1 Presses On As I noted above, Dyne Therapeutics was able to release positive data from its ongoing phase 1/2 ACHIEVE study ...

Use of DYNE-101 is leading to improvements in muscle, and specifically finger, function in myotonic dystrophy type 1 patients, new data show.

Patients with myotonic dystrophy have smaller hearts, and lower systolic and diastolic blood pressures and pulse rates. They have impaired autonomic reflexes, measured by orthostatic, Valsalva ...