Shares of Sarepta Therapeutics have plunged again after the drugmaker reported a second death in connection with its gene ...

Duchenne muscular dystrophy causes progressive muscle weakness that can rob kids of their ability to walk by the time they’re teenagers, and many don’t live well into their 30s. It affects an ...

The doctor may use different tests to check for conditions that can cause muscle weakness ... hard when your child loses strength and can’t do the things other kids can do. Muscular dystrophy ...

What Is Duchenne Muscular Dystrophy ... As they get older, your child might have other symptoms, including: The muscle problems can cause cramps at times, but in general, DMD isn’t painful.

The therapy can be used in 4- and 5-year-olds with the degenerative muscle disease, the agency announced June 22. Duchenne muscular dystrophy, the most common form of the muscle disease ...

The two brothers have Duchenne muscular dystrophy — a rare, inherited muscle-wasting disorder that has no cure. "Caleb stopped walking in December of '23, so a little over a year ago.

Parents of children living with muscular dystrophy say better expertise ... Another family from Barry, south Wales, who also have a young child living with Duchenne, said there is a better care ...

About seven months after her daughter was born, Zoey was diagnosed with the James type of Spinal Muscular Atrophy ... it works like any other kid her age." Zoey's condition requires weekly ...

Early diagnosis of rare diseases like Spinal Muscular Atrophy (SMA ... Caregivers should be vigilant if they notice their child struggling with these basic functions, as these symptoms can ...