suppress mutant hemoglobin, and supply functional adult hemoglobin, the researchers developed an approach that could produce more hemoglobin through a single vector. Researchers at Children's ...

The expression of β-globin leads to the formation of adult hemoglobin, the principal form ... BCL11A-shmiR Trial in progress Reni-cel (Editas Medicine) Sickle cell disease NCT04853576 Cas12 ...

suppress mutant hemoglobin, and supply functional adult hemoglobin, the researchers developed an approach that could produce more hemoglobin through a single vector. The results were published in ...