Childhood-onset striatonigral degeneration is a rare genetic disorder that robs children of the ability to walk and speak by ...

Marks’ resignation leaves the field without a regulator many view as “integral” to its progress over the last decade.

Here is our list of the 11 Best Gene Therapy Stocks to Buy According to Analysts.

The first clinical trial of a generative AI therapy bot suggests it was as effective as human therapy for people with ...

Three patients living with hypertrophic cardiomyopathy have had their disease classification downgraded following a single ...

The HFpEF Summit is a biannual, two-day meeting bringing together internationally recognized leaders in the clinical, biological, and translational study of HFpEF. This summit focused on the latest ...

Gene Therapy Loses Luster as Investors Eye Quicker Returns From Weight-Loss Drugs By Deena Beasley (Reuters) -Gene therapy, ...

Although cystic fibrosis is a single gene mutation, there are more than 1,000 different ways the CFTR gene can mutate in ...

From reproductive rights to climate change to Big Tech, The Independent is on the ground when the story is developing.

Provides update on the Company’s transformation and promising portfolio of innovative gene therapy treatments for inherited retinal ...

Inherited retinal degeneration (IRD) encompasses various disorders characterized by progressive loss of retinal photoreceptor cells, ultimately ...

Base editing corrected a mutation that causes macular degeneration, highlighting the potential of gene therapy to treat ...