For people living with rare genetic diseases – many of which can be debilitating or life-threatening – the need for innovative treatments is urgent. Only 5% of the 7,000 known rare diseases ...

Gene delivery is a process by which foreign DNA is transferred to host cells for applications such as genetic research or gene therapy. Gene delivery methods can be mechanical (e.g. microinjection ...

Common measurements for modified adeno-associated viruses (AAVs), a gene therapy delivery method, showed substantial ...

Researchers are making strides in improving gene therapies for genetic diseases, particularly chronic kidney disease, using adeno-associated virus, or AAV, vectors. While AAV-based treatments have ...

The global gene transfer technologies market, valued at US$3.63 billion in 2023, is forecasted to grow at a robust CAGR of 9.7%, ...

CRISPR is a powerful gene-editing tool that holds enormous potential for treating genetic diseases by allowing scientists to ...

In a new study, scientists combined strategies to deliver energy-disrupting gene therapy using ... in targeted anti-cancer therapy development. The foundation for the delivery system in this ...

Jay Rosanelli, CEO at Syenex, added: "This joint effort showcases the role of collaborative science in accelerating the ...

Undervalued biotech company Regenxbio Inc. shows promise with cutting-edge gene therapy technology for AMD and MPS II. Click ...

MSC-based strategies should provide practical advantages ... their activities might be further enhanced via targeted gene therapy Delivery of MSCs might be achieved either by direct intra ...