Javed Shaikh, Director of RWE & HEOR, Axtria, explains how harnessing next-generation sequencing and AI-powered analytics ...

Childhood-onset striatonigral degeneration is a rare genetic disorder that robs children of the ability to walk and speak by ...

These findings raise the question of whether retroviral VEGF gene therapy is useful for therapeutic ‘angiogenesis’ without risking ‘angioma-genesis’. Overexpression of VEGF may lead to an ...

To help improve gene therapy, a multidisciplinary team has generated a comprehensive atlas that researchers can use to select ...

Gene therapy, a technique that is revolutionizing the treatment of multiple genetic conditions, including eye and muscle diseases and blood disorders, requires efficient and specific delivery of the ...

Sangamo Therapeutics has stacked up $18 million cash from Eli Lilly in a licensing deal that will let the pharma use the ...

The findings were published in the New England Journal of Medicine. Cholesterol-Lowering Gene Therapy Shows Early Promise in First Human Trial Phase 2 trials are primarily used to further test a ...

Marks’ resignation leaves the field without a regulator many view as “integral” to its progress over the last decade.

BEAM-302's reparative technique separates it from many other CRISPR trials, which often try instead to completely knock out a dysfunctional gene. For example, Wave’s GSK-partnered therapy ...

Sineugene Therapeutics Co. Ltd. has obtained IND clearance from the FDA for SNUG-01, a first-in-class tripartite motif ...