Congenital hearing loss refers to impaired auditory function that occurs due to genetic causes. GJB2 is the gene responsible ...

Shares of Sarepta Therapeutics have struggled for the past year due to concerns about the commercial potential of its gene ...

It will be driven by significant advancements in gastrointestinal disorders treatments. The global cell and gene therapy (CGT ...

Childhood-onset striatonigral neurodegeneration robs children of the ability to walk and talk by age five. Researchers at ...

The Department of Health - Abu Dhabi (DoH), the regulator of the healthcare sector in the emirate, has announced the ...

Gene Therapy Loses Luster as Investors Eye Quicker Returns From Weight-Loss Drugs By Deena Beasley (Reuters) -Gene therapy, ...

Although cystic fibrosis is a single gene mutation, there are more than 1,000 different ways the CFTR gene can mutate in ...

A patient has died while taking a closely watched gene therapy for muscular dystrophy. Sarepta Therapeutics announced the ...

The death of a 16-year-old boy evokes a lengthy battle to realize the benefit of cutting-edge gene therapy while also ...

The rapid development of gene therapy options for treating neuromuscular diseases has created new therapeutic options but ...

A comprehensive approach, including robust preclinical research and a streamlined regulatory process, is the key ...

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