Dystrophin's isoforms are thought to contribute variably to neuropsychiatric disorders, behavioral disorders, and ...

Cardiac complications in Duchenne muscular dystrophy (DMD) are the result of cardiac muscle involvement that accompanies the ...

Satellos Bioscience Chief Scientific Officer discusses early-stage trials of the company's Duchenne muscular dystrophy drug, ...

Deramiocel 即将上市的背后，是全球 DMD 创新治疗版图的深刻变革。除了传统的糖皮质激素及当下多款上市的 ASO 药物外，Elevidys 等 AAV 基因疗法的获批则代表着 DMD ...

Advancements in gene therapy for Duchenne muscular dystrophy (DMD) have improved the outlook for some patients, but further ...

In many genetic diseases, a small error in the DNA code can have devastating effects. These errors, called nonsense mutations ...

Repurposing existing therapies may help slow muscle weakness in patients with Duchenne muscular dystrophy, a new study ...

A farmer living with a degenerative disease has shared how he adapted life on the farm to overcome the challenges of his ...

Use precise geolocation data and actively scan device characteristics for identification. This is done to store and access ...

A 46-year-old woman with type 1 myotonic dystrophy (DM1) presented to the emergency department with dyspnea and palpitations.