Base editing corrected a mutation that causes macular degeneration, highlighting the potential of gene therapy to treat ...

Sebastien Beauzile, 21, became the first person in New York state to be made symptom-free of sickle cell disease after ...

In the last year, some drugmakers have pulled back from the sector, including Pfizer, which recently stopped selling its gene ...

Childhood-onset striatonigral degeneration is a rare genetic disorder that robs children of the ability to walk and speak by ...

Although cystic fibrosis is a single gene mutation, there are more than 1,000 different ways the CFTR gene can mutate in ...

Credit: Artur Plawgo / Science Photo Library via A 21-year-old man has become the first person in New York—and ...

Congenital hearing loss refers to impaired auditory function that occurs due to genetic causes. GJB2 is the gene responsible ...

With a storied history in vaccine development, India's Bharat Biotech is shaking things up and answering the call of advanced ...

This approval was followed by Takeda Pharmaceuticals’ Alofisel (darvadstrocel), which received approval from the European Medicines Agency in 2018 and from Japan’s Pharmaceuticals and Medical Devices ...

Cell-free systems, which can express an easily detectable protein with a DNA or mRNA template without constraints of living ...

OXB honoured at 2025 CDMO Leadership Awards in 'Cell & Gene Therapy – Global' category Oxford, UK – 21 March 2025: OXB (LSE: ...

While the allogeneic vs autologous debate continues in the cell therapy field, research on in vivo therapies is drawing ...