There are only a handful of kids in the world with Lucy's disorder, which is called PGAP-3 CDG. There's no way to treat it. Sponsor Message In principle, CRISPR, the gene-editing technique that ...

They would use a technology known as CRISPR, a personalized gene-editing therapy, to find the one uniquely mutated gene out of 20,000 in his little body, and fix it. KJ subsequently received three ...

An infant in Philadelphia has been successfully treated with a customized Crispr gene-editing therapy for a rare and deadly disease, doctors reported Thursday—a breakthrough in the futuristic ...

Jason Mast is a general assignment reporter at STAT focused on the science behind new medicines and the systems and people that decide whether that science ever reaches patients. You can reach ...

And Lucy does, some days, suffer a lot.” There are only a handful of kids in the world with Lucy’s disorder, which is called PGAP-3 CDG. There’s no way to treat it. In principle, CRISPR, the ...